Luk Vandenberghe, PhD

Associate Professor of Ophthalmology, Massachusetts Eye and Ear Infirmary
In vitro and in vivo rescue of aberrant splicing in CEP290-associated LCA by antisense oligonucleotide delivery.
Authors: Authors: Garanto A, Chung DC, Duijkers L, Corral-Serrano JC, Messchaert M, Xiao R, Bennett J, Vandenberghe LH, Collin RW.
Hum Mol Genet
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AAV9 targets cone photoreceptors in the nonhuman primate retina.
Authors: Authors: Vandenberghe LH, Bell P, Maguire AM, Xiao R, Hopkins TB, Grant R, Bennett J, Wilson JM.
PLoS One
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The pleiotropic effects of natural AAV infections on liver-directed gene transfer in macaques.
Authors: Authors: Wang L, Calcedo R, Wang H, Bell P, Grant R, Vandenberghe LH, Sanmiguel J, Morizono H, Batshaw ML, Wilson JM.
Mol Ther
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Novel adeno-associated virus serotypes efficiently transduce murine photoreceptors.
Authors: Authors: Allocca M, Mussolino C, Garcia-Hoyos M, Sanges D, Iodice C, Petrillo M, Vandenberghe LH, Wilson JM, Marigo V, Surace EM, Auricchio A.
J Virol
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