Luk Vandenberghe, PhD

Associate Professor of Ophthalmology, Massachusetts Eye and Ear Infirmary
Gene therapy restores auditory and vestibular function in a mouse model of Usher syndrome type 1c.
Authors: Authors: Pan B, Askew C, Galvin A, Heman-Ackah S, Asai Y, Indzhykulian AA, Jodelka FM, Hastings ML, Lentz JJ, Vandenberghe LH, Holt JR, Géléoc GS.
Nat Biotechnol
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Retinal gene therapy coming of age.
Authors: Authors: Cepko CL, Vandenberghe LH.
Hum Gene Ther
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Naturally occurring singleton residues in AAV capsid impact vector performance and illustrate structural constraints.
Authors: Authors: Vandenberghe LH, Breous E, Nam HJ, Gao G, Xiao R, Sandhu A, Johnston J, Debyser Z, Agbandje-McKenna M, Wilson JM.
Gene Ther
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AAV as an immunogen.
Authors: Authors: Vandenberghe LH, Wilson JM.
Curr Gene Ther
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