Luk Vandenberghe, PhD
Associate Professor of Ophthalmology, Massachusetts Eye and Ear Infirmary
AAV-ID: A Rapid and Robust Assay for Batch-to-Batch Consistency Evaluation of AAV Preparations.
Authors: Authors: Pacouret S, Bouzelha M, Shelke R, Andres-Mateos E, Xiao R, Maurer A, Mevel M, Turunen H, Barungi T, Penaud-Budloo M, Broucque F, Blouin V, Moullier P, Ayuso E, Vandenberghe LH.
Mol Ther
View full abstract on Pubmed
Mol Ther
View full abstract on Pubmed
Gene therapy: charting a future course--summary of a National Institutes of Health Workshop, April 12, 2013.
Authors: Authors: O'Reilly M, Federoff HJ, Fong Y, Kohn DB, Patterson AP, Ahmed N, Asokan A, Boye SE, Crystal RG, De Oliveira S, Gargiulo L, Harper SQ, Ikeda Y, Jambou R, Montgomery M, Prograis L, Rosenthal E, Sterman DH, Vandenberghe LH, Zoloth L, Abedi M, Adair J, Adusumilli PS, Goins WF, Gray J, Monahan P, Popplewell L, Sena-Esteves M, Tannous B, Weber T, Wierda W, Gopal-Srivastava R, McDonald CL, Rosenblum D, Corrigan-Curay J.
Hum Gene Ther
View full abstract on Pubmed
Hum Gene Ther
View full abstract on Pubmed
Gene therapy in a humanized mouse model of familial hypercholesterolemia leads to marked regression of atherosclerosis.
Authors: Authors: Kassim SH, Li H, Vandenberghe LH, Hinderer C, Bell P, Marchadier D, Wilson A, Cromley D, Redon V, Yu H, Wilson JM, Rader DJ.
PLoS One
View full abstract on Pubmed
PLoS One
View full abstract on Pubmed
Tailoring the AAV vector capsid for gene therapy.